FUNDED ADDITIONAL POST-DOC FELLOW FOCUSED ON ASMD RESEARCH PROJECTS. CONTINUED SUPPORTING MULTIPLE SINGLE PATIENT INVESTIGATOR-INITIATED/EXPANDED ACCESS EXPERIMENTAL TREATMENTS FOR ASMD. FUNDED CNS SPECIFIC BIOMARKER STUDY TO IDENTIFY THE STRUCTURE OF A POTENTIAL NOVEL BIOMARKER FOR ASMD. EXTENDED DATA COLLECTION FOR OUR ASMD ACCELERATE STUDY FOR 2 ADDITIONAL YEARS. BEGAN CHARACTERIZING ASMKO IPS CELL LINE DEVELOPED IN 2023. FUNDED MULTIPLE IN VITRO AND IN VIVO DRUG REPURPOSING STUDIES FOR ASMD. DID FOLLOW UP FILMING WITH ASMD FAMILIES FOR DISEASE AWARENESS VIDEOS. HAD FIRST PATENT GRANTED IN THE U.S. FOR POTENTIAL ASMD TREATMENT.
